Families with Huntington’s need this to be true more than most. The devastating neurodegenerative disease is caused by a CAG ...

Qure N.V. (NASDAQ:QURE) surged around 15% in early trading on Friday after the company said it has secured a Type A meeting ...

Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, today announced the ...

Shares of UniQure were higher after the gene therapy company said it had scheduled a Type A meeting with the Food and Drug Administration to discuss a Biologics License Application for the company's ...

For the first time, scientists have successfully treated someone suffering from Huntington's disease, a fatal genetic illness ...

UCL and uniQure report the first treatment to slow Huntington’s disease with gene therapy AMT-130. High-dose patients had 75% less progression over three years compared with standard care. uniQure ...

Huntington's is an inherited disease caused by a mutation in a single gene that causes a progressive breakdown of the brain's nerve cells. This degeneration in the brain may have a wide impact on a ...

Researchers have implicated a new gene in the progression of Huntington's disease in a brain organoid model. The gene may contribute to brain abnormalities much earlier than previously thought. Six ...

NEW YORK, Sept. 25, 2025 /PRNewswire/ -- The Hereditary Disease Foundation (HDF) is proud to announce its new name, Huntington's Disease Foundation, with the same unwavering commitment to fund ...

Huntington's disease (HD) is a hereditary neurodegenerative disorder caused by a mutation in the gene called huntingtin on chromosome 4. HD is inherited in an autosomal dominant fashion, so that each ...

Huntington's Disease burdens caregivers in India, facing financial strain and limited support amid widespread underdiagnosis ...