An international team of scientists has designed a new type of therapy to target the mutant toxic RNA that causes myotonic ...

The U.S. Food and Drug Administration has awarded orphan drug status to Atossa Therapeutics' (Z)-endoxifen for Duchenne ...

What is strength? Columnist Patrick Moeschen believes it's the act of persevering through events that are beyond our control.

My family and I are part of a community of boys, men, and families living with Duchenne muscular dystrophy. That community extends far beyond the U.S., where we live. Families uniquely experience ...